Gene therapy, a technique that is revolutionizing ... delivery was in different tissues, down to the level of the individual cells.” The approach led the researchers to discover new insights on AAV ...

as it suggests that gene therapy could be effective even in advanced stages of the disease," explains Alejandro Brao, researcher at the Department of Biochemistry and Molecular Biology and INc-UAB ...

A recent study led by the Universitat Autònoma de Barcelona (UAB) demonstrates the potential of gene therapy to restore motor capacity in an ultra-rare disease, Megalencephalic Leukoencephalopathy ...