CRISPR Therapeutics’ partner Vertex reported that more than 65 treatment centers have been activated for the gene therapy ...

To help achieve more precise control of gene therapy, engineers have designed a new control circuit that can keep gene expression levels within a target range. The method could be used to deliver ...

A new gene therapy reversed heart failure in pigs by repairing heart function through cBIN1, showing major promise for future ...

a unique and innovative co-development partnership with the NPHP1 Family Foundation to create an AAV-based gene replacement therapy for retinal dystrophy caused by mutations in the NPHP1 ...

While gene therapy economics are multifactorial ... And, if yes, can the price point be brought down to a level that healthcare systems and payers can manage in large numbers, especially when ...

A Johnson & Johnson gene therapy in development for an inherited vision-loss disorder has failed a Phase 3 study, the latest clinical research setback for a rare eye disease that so far has no FDA ...

Over the last 15 years, I have witnessed how cell and gene therapy (CGT ... Optimize therapy efficiency and manufacturability at the biological level. • Develop financial strategies alongside ...

By studying basic biology in our cells ... Center for Virology and Vaccine Research at BIDMC, member of the Gene and Cell Therapy Institute at Mass General Brigham, and member of the faculty ...

The two met and married at Harvard Medical School—Maguire was becoming an eye surgeon, and Bennett, who also had a PhD in developmental biology, was about to enter the new field of gene therapy.

Odylia Therapeutics, a nonprofit (501(c)3) biotechnology company dedicated to advancing treatments for rare diseases, today announced its latest pipeline project: a unique and innovative ...