As mothers of children with this disease, we have wept helplessly in recent months as friends — fellow members of a club we ...

Oasis fan Mark Chapman was left deeply frustrated at the band's iconic reunion gig in Manchester's Heaton Park as 'non-disabled' gig-goers 'took over' the accessible area ...

While genetic testing could not confirm Duchenne muscular dystrophy, a muscle biopsy at UCLA did. "He could see that he was declining, and that it was getting worse," said Stephanie.

After second Sarepta death, Duchenne muscular dystrophy community is racked by recrimination and worry ‘This kid died from the same thing we’re trying to fight off right now,’ one parent says ...

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

Delandistrogene Moxeparvovec Gene Therapy in Individuals With Duchenne Muscular Dystrophy: Evidence in Focus. Neurology , 2025; 104 (11) DOI: 10.1212/WNL.0000000000213604 Cite This Page : ...

DMD was first described by French neurologist Guillaume Benjamin Amand Duchenne in the 1860s. However, until the 1980s, little was known about the causes of any type of muscular dystrophy.

Biotech firm Sarepta Therapeutics said that a second patient died after receiving its gene therapy to treat Duchenne muscular dystrophy, the latest drug to draw scrutiny after winning fast ...

The one-time treatment is approved for children with a genetic variant of Duchenne’s muscular dystrophy, which causes weakness, loss of mobility and early death in males.

Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying therapies using gene replacement, antisense oligonucleotides, and gene ...

The Sapp family pose for a photo while on a family vacation. Amber Sapp, a St. Petersburg resident, is a physical therapist and mom to 18-year-old Garrett, who lives with Duchenne muscular dystrophy.