Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

In March 2025, Vertex Pharmaceuticals Incorporated announced a study is to evaluate the safety, and tolerability and efficacy ...

The genetic condition cystic fibrosis had no treatments on the NHS before 2019 and a Daily Express campaign - now a miracle ...

The Foundation’s National Volunteer Advocacy Committee provides guidance and support to further strengthen and enhance the ...

Among the candidates listed for lung transplant, those with an indication of CF decreased from 13.3% in the pre–highly ...

Use precise geolocation data and actively scan device characteristics for identification. This is done to store and access ...

UnitedHealth Group's pharmacy benefit manager, Optum Rx, said on Wednesday it would ease requirements to get insurance ...

The Hospital for Sick Children. "Newly uncovered mechanism could drive next-gen cystic fibrosis treatments." ScienceDaily. ScienceDaily, 13 March 2025. <www.sciencedaily.com / releases / 2025 / 03 / ...

Reports Q4 grant revenue $1.2M vs $1.5M last year. “During the fourth quarter, we achieved another significant clinical milestone with ...

UnitedHealth Group Inc.’s pharmacy benefit manager, Optum Rx, will ease renewal requirements for certain long-term ...

Phase 1 MAD dosing completed for SION-451 and final MAD cohort of SION-719 planned; Interim data in healthy volunteers show potential to provide ...