Research shows Black cystic fibrosis patients are more likely than their white counterparts to be among the 10% who don’t benefit from modulator therapies. Can a gene therapy work no matter the ...

Vertex Pharmaceuticals on Monday reported disappointing first-quarter earnings impacted by weaker-than-expected sales of its ...

Vertex Pharmaceuticals is pressing pause on a phase 1/2 cystic fibrosis (CF) trial over a tolerability issue while reporting ...

May is Cystic Fibrosis Awareness Month - learn about this genetic condition causing thick mucus and organ damage.

Antimicrobial resistance, in which germs like bacteria and fungi no longer respond to medicines, is a rising global threat.

Battling a rare mutation of cystic fibrosis, Emily Kramer-Golinkoff fights for her life — and for gene therapies that offer ...

Vertex Pharmaceuticals missed Wall Street estimates for quarterly results on Monday, due to lower-than-expected sales of its ...

People with diseases caused by rare mutations have fewer options and poorer prospects than other patients despite rapid ...

Vertex Pharmaceuticals on Monday reported disappointing first-quarter earnings impacted by weaker-than-expected sales of its drugs for cystic fibrosis ... from a gene therapy for sickle cell ...