Neurocrine Biosciences has handed back two discovery-stage gene therapy programs to Voyager Therapeutics, although the ...

Sarepta has submitted a request to the FDA to include the death case in Elevidys’ label, and the agency plans to review the ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...

Ophthalmology Times - ophthalmology news, articles, and events in a timely and accurate manner for members of the ophthalmic ...

A vocal opponent of his predecessor Peter Marks, Vinay Prasad will now lead the office tasked with reviewing some genetic ...

The designation was granted based on preliminary clinical evidence from an ongoing dose-escalation open-label Phase I/II ...

As scientists explore treating genetic disorders before birth, the promise of foetal gene therapy is growing—but there are ...

Vanotech is the sponsor representative and is responsible for the clinical development programme for the therapy in the US.

The US Food and Drug Administation (FDA) has approved BlackfinBio Limited’s Phase 1/2 clinical trial for its novel ...

Pacira BioSciences has revealed that PCRX-201 has demonstrated improvements in individuals with knee osteoarthritis in a Phase I trial.

The LUMEOS trial enrolled 95 patients, 58 of whom received either a low or high single dose of botaretigene sparoparvovec (bota-vec), an investigational gene therapy that uses an adeno-associated ...

Presentation to Highlight Genprex's Study of Reqorsa Gene Therapy in Combination with Tecentriq ® for the Treatment of Extensive Stage Small Cell Lung Cancer AUSTIN, Texas, April 24, 2025 ...