Acute flaccid paralysis in children is a medical emergency that can progress to respiratory failure within hours or days, ...

Of all the autoimmune diseases out there, Guillain-Barre syndrome is definitely one of the less common. This condition, which affects the body's nerves and causes muscle weakness that develops into ...

Researchers are working overtime to develop therapies that, for the first time, specifically target Guillain-Barré Syndrome. That's welcome news.

With the FDA recently rejecting a drug application that aims to help those living with Barth Syndrome, one Bay Area family is frustrated by the delay of approved treatments in the rare disease ...

Investing.com -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) stock gained 2.2% premarket after the company announced that its experimental treatment for Angelman syndrome received Breakthrough ...

A Back Mountain resident awaiting sentencing on a manslaughter charge for failing to help her boyfriend during a fatal drug overdose pleaded guilty Wednesday in an unrelated drug case. William John… ...

The drug, elamipretide, targets cardiolipins, a molecule in the mitochondria that is a key source for the gene defect. It’s the only drug for Barth Syndrome clinical trials.

Hopes have risen for a new treatment for severe childhood epilepsy Dravet syndrome, on the back of new data for Biogen and Stoke's zorevunersen ...

A Hanover Twp. man has been sentenced to 15 years in federal prison on drug trafficking and weapons charges, according to the U.S. Attorney’s Office. Christopher Essameddin Birry, 43, was con… ...

A digoxin-induced AV block usually improved (28 of 39) after withdrawal of the drug. Roughly half of the patients with drug-induced AV block underwent permanent PM implantation.

Hunterdon County Prosecutor Renée Robeson announced Thursday, that Leonard R. Contreras, 26, of South Amboy, New Jersey, has been sentenced.