Uncertainty around ELEVIDYS sales impact Sarepta Therapeutics, Inc. Click here to find out why I downgraded SRPT stock to a ...

The CHMP recommends conditional marketing authorization for Duvyzat to treat Duchenne muscular dystrophy in patients aged 6 ...

Capricor Therapeutics said on Monday the U.S. Food and Drug Administration (FDA) plans to convene a panel of outside experts ...

A new study led by researchers at the Hospital for Special Surgery (HSS) suggests that currently available therapies may help ...

Sarepta has submitted a request to the FDA to include the death case in Elevidys’ label, and the agency plans to review the ...

A new study led by researchers at Hospital for Special Surgery (HSS) suggests that currently available therapies may help ...

Country superstar Alan Jackson has been battling Charcot-Marie-Tooth disease for more than a decade, but he didn't go public ...

whether there's something targeted to their exact genetic mutation. An example of that would be a stop code on read through for Duchenne muscular dystrophy, which was a treatment that was ...

Muscular dystrophy, as a category, is quite diverse. There's dozens of disorders that ... But unfortunately, none are a cure, and we still have very severe symptoms that we're managing with ...