Amyotrophic lateral sclerosis (ALS) - which you may know as the disease that affected Stephen Hawking - is a fatal ...

Sarepta Therapeutics suffered another major setback on Friday as Europe's drug regulator decided not to recommend the ...

Amyotrophic lateral sclerosis (ALS) is a fatal neurodegenerative disease that causes progressive muscle weakness. A research ...

Discover how CRISPR gene editing is creating personalized cancer therapies, enhancing immunotherapy, and offering new hope ...

During a severe heart attack many heart muscle cells die and are replaced by scar tissue to stabilize the heart wall.

The pharma sees the drug, gefurulimab, as a more convenient, self-administered alternative to the infused medicines it sells ...

Our study identifies FOXK2 as a novel pathogenic gene for congenital myopathy with ptosis and highlights its essential role in skeletal muscle development and mitochondrial homeostasis, offering ...

Many cancer survivors struggle with muscle weakness, which can be so profound that they may have difficulties walking up a couple of flights of stairs or going shopping for groceries on their own.

This week's episode covers Merck's latest $10B acquisition, advances in virtual cell AI benchmarking, and promising restored hearing results from the AAV-OTOF gene therapy trial.

The first hemophilia B patient in Germany received gene therapy Hemgenix, covered by public healthcare with efficacy-tied reimbursement.

UC Berkeley and Caltech researchers identified a gene circuit in zebrafish that allows heart regeneration after injury. Using CRISPR, they pinpointed key genes like egr1 that may reactivate heart ...

Zebrafish have the rare ability to regenerate their heart muscle after major damage, unlike humans. Researchers have now ...