News

The New England Journal of Medicine10d
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1
Damaging variants in ITGB2, which encodes CD18, cause leukocyte adhesion deficiency ... blood mononuclear cells and sustained CD18 neutrophil expression of at least 10% of the normal expression ...
No more 'death sentence': 100% survival rate achieved in gene therapy trial
"It's a momentous breakthrough for families facing this devastating disease," said Dr. Claire Booth, leader of the London ...
'My son has death sentence disease that should've killed him before 2nd birthday'
Eisa Hussain was born with a condition meaning his body could not fight off infections and he was expected to die before the ...
London hospital gene therapy breakthrough gives boy with ‘death sentence’ disease a normal life
A boy with an ultra-rare immune disease which can carry a “death sentence” is living a normal life after taking part in a ...
The Independent on MSN9d
Breakthrough gene therapy gives boy with ‘death sentence’ disease a normal life
A boy with an ultra-rare immune disease which can carry a “death sentence” is living a normal life after taking part in a ...
Boy, 4, given 'death sentence' from rare disease receives incredible breakthrough
Eisa Hussain was born with a severe form of leukocyte adhesion deficiency 1 (LAD-1), which can carry a "death sentence" if ...
Seeking Alpha18d
Trodelvy® Plus Keytruda® Demonstrates a Statistically Significant and Clinically Meaningful Improvement in Progression Free Survival in Patients With Previously Untreated PD ...
In the pooled safety population, the most common (≥ 25%) adverse reactions including laboratory abnormalities were decreased leukocyte count (84%), decreased neutrophil count (75%), decreased ...
Manchester Evening News9d
Boy, 4, given 'death sentence' from rare disease receives incredible breakthrough
Eisa Hussain was born with a severe form of leukocyte adhesion deficiency 1 ... of a specific subset of white blood cells called neutrophils that are the "first line of defence" when the body ...
Boy with ‘death sentence’ disease living a normal life after breakthrough gene therapy
A four-year-old boy with a life-threatening immune disease is now living a normal life thanks to a pioneering gene therapy ...
Express & Star10d
Breakthrough gene therapy gives boy with ‘death sentence’ disease a normal life
Children born with a severe form of leukocyte adhesion deficiency 1 ... surface of a specific subset of white blood cells called neutrophils. They blood cells have been likened to the “first ...