Angelman Syndrome is a rare genetic condition that effects one in every 20,000 kids. GOP Plan to Permanently Rename Wildlife Refuge 11 Expensive Steakhouse Chains That Aren't Worth The Price Tag US ...

Learn more about whether BioCryst Pharmaceuticals, Inc. or Ultragenyx Pharmaceutical Inc. is a better investment based on ...

Find Gene Editing Therapy Latest News, Videos & Pictures on Gene Editing Therapy and see latest updates, news, information from NDTV.COM. Explore more on Gene Editing Therapy.

“Having said that a number of stocks have bounced back pretty strongly and if you look at ProMedicus (ASX:PME) it hit a low of $161.64 on April 7th and has rallied back to over $270, up 67% in a ...

Sean Penn appeared on “The Louis Theroux Podcast” and declared Jennifer Lawrence to be “probably the last movie star.” Penn ...

Delores Flanders and her family are hosting a fundraiser at Boutwell’s Bowling Center in Concord to raise money for the ...

Prader-Willi syndrome is a rare genetic disease that causes poor feeding in infancy but later triggers insatiable hunger.

Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) released its 2024 Impact Report today, which covers the company's approach to corporate responsibility.

Encoded Therapeutics Inc., a clinical-stage biotechnology company developing genetic medicines for severe central nervous system (CNS) disorders, today announced the results of preclinical studies ...

Mavrix Bio has received IND clearance from the FDA for MVX-220, an investigational AAV gene therapy for the treatment of Angelman syndrome. The company expects to initiate its first-in-human study, ...