Rocket Pharmaceuticals has shared early data from three patients that tie its gene therapy for an inherited heart disease to ...

News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, ...

Q1 2025 Earnings Call Transcript May 15, 2025 Taysha Gene Therapies, Inc. reports earnings inline with expectations. Reported ...

AviadoBio has opened the multi-centre Phase I/II ASPIRE-FTD trial in the UK, aimed at assessing the gene therapy candidate ...

AGC Biologics has collaborated with Quell Therapeutics to advance the development of several T-regulatory (Treg) cell therapy ...

The UNC technology, developed by Pediatrics Professor Chengwen Li, M.D., Ph.D., uses adeno-associated viruses (AAVs) to ferry ...

Ophthalmology Times - ophthalmology news, articles, and events in a timely and accurate manner for members of the ophthalmic ...

Scientists sprinted to create personalized medicine for baby KJ powered by CRISPR, a powerful gene-editing technology that won the Nobel Prize five years ago.

In a world first, scientists used CRISPR to fix a baby's unique genetic mutation. The report offers hope for personalized ...

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec, the American Academy of ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.