Uncertainty around ELEVIDYS sales impact Sarepta Therapeutics, Inc. Click here to find out why I downgraded SRPT stock to a ...

Sarepta has submitted a request to the FDA to include the death case in Elevidys’ label, and the agency plans to review the ...

Capricor Therapeutics said on Monday the U.S. Food and Drug Administration (FDA) plans to convene a panel of outside experts ...

The Sunday Times, a newspaper in western Australia, reports that Dr Hurst died by suicide last December at the age of 43, ...

A new study led by researchers at Hospital for Special Surgery (HSS) suggests that currently available therapies may help ...

The CHMP recommends conditional marketing authorization for Duvyzat to treat Duchenne muscular dystrophy in patients aged 6 ...

DMD is caused by a mutation in the dystrophin gene ... births—and leads to premature death due to respiratory and cardiac ...

Sixty-four cases of muscular dystrophy were diagnosed according ... were analyzed for changes within each treatment group and between groups. There was no significant improvement, subjective ...

Health experts have warned that vaping can cause irreversible damage to your lungs, following reports of 'popcorn lung'. Officially termed bronchiolitis obliterans, popcorn lung is a severe ...

The results of this study open the way for the development of treatments for the Disease, which currently has no fundamental cure, and are evaluated as demonstrating the innovativeness and ...

Over the past twelve months there has been significant advancements in cell gene therapy for inherited retinal dystrophy, with an FDA approval of Spark Therapeutics’ Voretigene – the first ...